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After Daybue’s Approval Acadia Pharmaceuticals’ Next Steps for the Rett Syndrome Community
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YouTubeXtalks
After Daybue’s Approval Acadia Pharmaceuticals’ Next Steps for the Rett Syndrome Community
Rett syndrome, a rare genetic disorder primarily affecting girls, causes severe physical and cognitive impairments. Dr. Kathie Bishop, Senior VP at Acadia Pharmaceuticals, discusses the recent FDA approval of Daybue (trofinetide), the first and only treatment for Rett syndrome. Daybue strengthens neuronal connections, addressing the core ...
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